Found 5 matching trials
Securing Access to Innovative Molecules in Oncology and Hematology for Children, Adolescents and Young Adults N/A It involves collecting safety and efficacy data, under the actual condition...
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University Hospital Antwerp
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Drug Repurposing for Mitochondrial Disorders Using iPSCs Derived Neural Cells N/A In this project, the investigators are using iPSC lines derived from patien...
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Universitätsklinikum Düsseldorf
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Acute Rhabdomyolysis and Muscle Pain Associated With Mutations in the LPIN1 Gene - A Retrospective Study Describing the Safety and Efficacy of Hydroxychloroquine Sulfate Given on a Compassionate Basis to Patients Suffering From Lipin-1 Deficiency N/A Lipin-1 deficiencies are responsible for severe rhabdomyolysis and muscle p...
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Hôpital Necker-Enfants Malades
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Securing Access to Innovative Molecules in Oncology and Hematology for Children, Adolescents and Young Adults N/A It involves collecting safety and efficacy data, under the actual condition...
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Molecular Profiling and Matched Targeted Therapy for Patients With Unresectable Advanced or Metastatic Melanoma PHASE2 This is a patient oriented translational research project aiming to improve...
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Westmead Hospital
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